Partial correction of cystinuria type A in mice via kidney-targeted transposon delivery
Open Access
- 21 July 2025
- journal article
- Published by Elsevier in Molecular Therapy Nucleic Acids
- Vol. 36 (3) , 102639
Abstract
No abstract availableKeywords
Funding Information
- National Institutes of Health (BX002797)
- National Institutes of Health (BX004845)
- National Institutes of Health (EB033676)
- National Institute of Diabetes and Digestive and Kidney Diseases (DK093660)
- Vanderbilt O’Brien Kidney Center
- U.S. Department of Veterans Affairs (BX004845)
- U.S. Department of Veterans Affairs (BX002797)
- U.S. Department of Veterans Affairs (BX004285)
- U.S. Department of Veterans Affairs (BX002190)
This publication has 30 references indexed in Scilit:
- Kidney-specific transposon-mediated gene transfer in vivoScientific Reports, 2017
- piggyBac-ing models and new therapeutic strategiesTrends in Biotechnology, 2015
- Hereditary causes of kidney stones and chronic kidney diseasePediatric Nephrology, 2013
- Hyperactive piggyBac Gene Transfer in Human Cells and In VivoHuman Gene Therapy, 2012
- Cystinuria: an inborn cause of urolithiasisOrphanet Journal of Rare Diseases, 2012
- A hyperactive piggyBac transposase for mammalian applicationsProceedings of the National Academy of Sciences, 2011
- Pathophysiology and treatment of cystinuriaNature Reviews Nephrology, 2010
- Cystinuria in childhood and adolescence: recommendations for diagnosis, treatment, and follow-upPediatric Nephrology, 2004
- Random peptide libraries displayed on adeno-associated virus to select for targeted gene therapy vectorsNature Biotechnology, 2003
- Rapid analysis of amino acids using pre-column derivatizationJournal of Chromatography B: Biomedical Sciences and Applications, 1984