Prognostic factors for the late onset Pompe disease with enzyme replacement therapy: From our experience of 4 cases including an autopsy case
Authors:
- Hiroshi KobayashiHKHiroshi Kobayashi
- Yohta ShimadaYSYohta Shimada
- Masahiro IkegamiMIMasahiro Ikegami
- Toshinao KawaiTKToshinao Kawai
- Ken SakuraiKSKen Sakurai
- Takashi UrashimaTUTakashi Urashima
- Masatoshi IjimaMIMasatoshi Ijima
- Masako FujiwaraMFMasako Fujiwara
- Eiko KaneshiroEKEiko Kaneshiro
- Toya OhashiTOToya Ohashi
- Yoshikatsu EtoYEYoshikatsu Eto
- Keiko IshigakiKIKeiko Ishigaki
- 1 May 2010
- journal article
- case report
- Published by Elsevier in Molecular Genetics and Metabolism
- Vol. 100 (1) , 14-19
Abstract
No abstract availableKeywords
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