Improved efficacy of FKRP AAV gene therapy by combination with ribitol treatment for LGMD2I
Authors:
- Marcela P. CataldiMarcela P. Cataldi
- Charles H. VannoyCVCharles H. Vannoy
- Anthony BlaeserABAnthony Blaeser
- Jason D. TuckerJTJason D. Tucker
- Victoria LeroyVLVictoria Leroy
- Raegan RawlsRRRaegan Rawls
- Jessalyn KillileeJKJessalyn Killilee
- Molly C. HolbrookMHMolly C. Holbrook
- Qi Long LuQLQi Long Lu
Open Access
- 1 November 2023
- journal article
- research article
- Published by Elsevier in Molecular Therapy
- Vol. 31 (12) , 3478-3489
Abstract
No abstract availableKeywords
Funding Information
- Atrium Health Foundation
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