Genetic therapies for neurological diseases
Open Access
- 3 October 2025
- journal article
- review article
- Published by Elsevier in Pharmacological Reviews
- Vol. 78 (1) , 100093
Abstract
No abstract availableKeywords
Funding Information
- UK Research and Innovation Medical Research Council (MR/S009434/1)
- UK Research and Innovation Medical Research Council (MR/S036784/1)
- UK Research and Innovation Medical Research Council (MR/R025134/1)
- UK Research and Innovation Medical Research Council (MR/T044853/1)
- UK Research and Innovation Medical Research Council (MR/V034758/1)
- UK Research and Innovation Medical Research Council (MR/Y008405/1)
- UK Research and Innovation Medical Research Council (MR/X008029/1)
- UK Research and Innovation Medical Research Council (MR/N026101/1)
- Jameel Education Foundation
- NIHR Great Ormond Street Hospital Biomedical Research Centre (562868)
- UK Research and Innovation (EP/Z000165/1)
- Rosetrees
- Wellcome Trust (204841/Z/16/Z)
- Wellcome Trust (223082/Z/21/Z)
- Wellbeing of Women
- United Kingdom Clinical Research Collaboration
- Cure Huntington's Disease Initiative
- National Institute for Health and Care Research
- UK Dementia Research Institute
- Sir Jules Thorn Charitable Trust
- Sparks
- European Research Council (EP/Z000165/1)
- LifeArc
- Great Ormond Street Hospital Children's Charity (V2403)
- Great Ormond Street Hospital Children's Charity (V4422)
- National Institutes of Health
- Great Ormond Street Hospital for Children
- CHDI Foundation Los Angeles
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