A Model for Spinal Muscular Atrophy Disease Registry for Iran
Open Access
- 1 August 2025
- journal article
- Published by National Academy of Sciences of Tajikistan in Payesh (Health Monitor) Journal
- Vol. 24 (4) , 439-455
Abstract
Objective(s): Spinal muscular atrophy is a rare genetic disease of neuromuscular and it is considered the main cause of death of newborns, which affects spinal motor neurons. The variety of degrees of this disease and the lack of a complete and integrated information recording system hinder the quality of providing care, early ...Keywords
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