Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase
Authors:
- Paul HarmatzPHPaul Harmatz
- Roberto GiuglianiRGRoberto Giugliani
- Ida Vanessa D. SchwartzISIda Vanessa D. Schwartz
- Nathalie GuffonNGNathalie Guffon
- Elisa Leão TelesETElisa Leão Teles
- M. Clara Sá MirandaMMM. Clara Sá Miranda
- J. Edmond WraithJWJ. Edmond Wraith
- Michael BeckMBMichael Beck
- Laila ArashLALaila Arash
- Maurizio ScarpaMSMaurizio Scarpa
- David KetteridgeDKDavid Ketteridge
- John J. HopwoodJHJohn J. Hopwood
- 1 August 2008
- journal article
- Published by Elsevier in Molecular Genetics and Metabolism
- Vol. 94 (4) , 469-475
Abstract
No abstract availableKeywords
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