Enzyme replacement therapy for mucopolysaccharidosis VI: long‐term cardiac effects of galsulfase (Naglazyme®) therapy
Open Access
- 5 June 2012
- journal article
- research article
- Published by Wiley in Journal of Inherited Metabolic Disease
- Vol. 36 (2) , 385-394
Abstract
Characteristic cardiac valve abnormalities and left ventricular hypertrophy are present in untreated patients with mucopolysaccharidosis type VI (MPS VI). Cardiac ultrasound was performed to investig...Keywords
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