Nusinersen for Type 1 Spinal Muscular Atrophy: A Father’s Perspective
- 1 October 2019
- journal article
- editorial
- Published by American Academy of Pediatrics (AAP) in Pediatrics
- Vol. 144 (4) , e20190226
Abstract
No abstract availableThis publication has 5 references indexed in Scilit:
- Nusinersen for Spinal Muscular AtrophyJAMA Pediatrics, 2018
- Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular AtrophyNew England Journal of Medicine, 2017
- Developmental milestones in type I spinal muscular atrophyNeuromuscular Disorders, 2016
- Observational study of spinal muscular atrophy type I and implications for clinical trialsNeurology, 2014
- Optimality score for the neurologic examination of the infant at 12 and 18 months of ageThe Journal of Pediatrics, 1999