Efficient in Vivo Manipulation of Alternative Pre-mRNA Splicing Events Using Antisense Morpholinos in Mice

This publication has 43 references indexed in Scilit:

• Fox-1 family of RNA-binding proteins
  Cellular and Molecular Life Sciences, 2009
• Octa-guanidine Morpholino Restores Dystrophin Expression in Cardiac and Skeletal Muscles and Ameliorates Pathology in Dystrophic mdx Mice
  Molecular Therapy, 2009
• Therapeutic Potential of Splice-Switching Oligonucleotides
  Oligonucleotides, 2009
• RNA and Disease
  Cell, 2009
• RNA repair restores hemoglobin expression in IVS2–654 thalassemic mice
  Proceedings of the National Academy of Sciences, 2009
• Expression of 24,426 human alternative splicing events and predicted cis regulation in 48 tissues and cell lines
  Nature Genetics, 2008
• Sustained Dystrophin Expression Induced by Peptide-conjugated Morpholino Oligomers in the Muscles of mdx Mice
  Molecular Therapy, 2008
• Antisense Masking of an hnRNP A1/A2 Intronic Splicing Silencer Corrects SMN2 Splicing in Transgenic Mice
  The American Journal of Human Genetics, 2008
• Intrasplicing coordinates alternative first exons with alternative splicing in the protein 4.1R gene
  The EMBO Journal, 2007
• Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
  Nature Medicine, 2006