Clinical Evaluation of N‐Acetyl‐l‐Leucine in Niemann–Pick Disease Type C: A Critical Perspective
Authors:
- 17 March 2025
- journal article
- Published by Wiley in Movement Disorders Clinical Practice
- Vol. 12 (5) , 592-593
Abstract
No abstract availableKeywords
This publication has 3 references indexed in Scilit:
- Trial of N -Acetyl- l -Leucine in Niemann–Pick Disease Type CNew England Journal of Medicine, 2024
- N -Acetyl- l -Leucine and Neurodegenerative DiseaseNew England Journal of Medicine, 2024
- Effects of acetyl-dl-leucine in patients with cerebellar ataxia: a case seriesJournal of Neurology, 2013