CRISPR deletion of the C9ORF72 promoter in ALS/FTD patient motor neurons abolishes production of dipeptide repeat proteins and rescues neurodegeneration
Open Access
- 7 April 2020
- journal article
- research article
- Published by Springer Nature in Acta Neuropathologica
- Vol. 140 (1) , 81-84
Abstract
No abstract availableFunding Information
- National Institutes of Health (R37NS057553, R01NS101986, R01NS093097, R21NS112766)
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