Targeted Gene Correction in Osteopetrotic-Induced Pluripotent Stem Cells for the Generation of Functional Osteoclasts
Authors:
- Sharon MuggeoSMSharon Muggeo
- Marianna PaulisMPMarianna Paulis
- Laura CrisafulliLCLaura Crisafulli
- Dario StrinaDSDario Strina
- Francesca FaggioliFrancesca Faggioli
- Camilla RecordatiCRCamilla Recordati
- Samantha ScaramuzzaSSSamantha Scaramuzza
- Eugenio ScanzianiESEugenio Scanziani
- Stefano ManteroSMStefano Mantero
Open Access
- 1 October 2015
- journal article
- research article
- Published by Elsevier in Stem Cell Reports
- Vol. 5 (4) , 558-568
Abstract
No abstract availableKeywords
This publication has 20 references indexed in Scilit:
- Targeted genome editing in human repopulating haematopoietic stem cellsNature, 2014
- Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic LeukodystrophyScience, 2013
- Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich SyndromeScience, 2013
- Amniocytes can serve a dual function as a source of iPS cells and feeder layersHuman Molecular Genetics, 2010
- Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemiaNature, 2010
- Efficacy of Gene Therapy for X-Linked Severe Combined ImmunodeficiencyNew England Journal of Medicine, 2010
- Committed osteoclast precursors colonize the bone and improve the phenotype of a mouse model of autosomal recessive osteopetrosisJournal of Bone and Mineral Research, 2010
- Gene Therapy for Immunodeficiency Due to Adenosine Deaminase DeficiencyNew England Journal of Medicine, 2009
- Treatment of Sickle Cell Anemia Mouse Model with iPS Cells Generated from Autologous SkinScience, 2007
- Defects in TCIRG1 subunit of the vacuolar proton pump are responsible for a subset of human autosomal recessive osteopetrosisNature Genetics, 2000