Cas9-induced single cut enables highly efficient and template-free repair of a muscular dystrophy causing founder mutation
Authors:
Open Access
- 5 February 2023
- journal article
- research article
- Published by Elsevier in Molecular Therapy Nucleic Acids
- Vol. 31, 494-511
Abstract
No abstract availableKeywords
This publication has 56 references indexed in Scilit:
- RNA-programmed genome editing in human cellseLife, 2013
- A Programmable Dual-RNA–Guided DNA Endonuclease in Adaptive Bacterial ImmunityScience, 2012
- Satellite cells are essential for skeletal muscle regeneration: the cell on the edge returns centre stageDevelopment, 2012
- An absolute requirement for Pax7-positive satellite cells in acute injury-induced skeletal muscle regenerationDevelopment, 2011
- Non-Proteolytic Functions of Calpain-3 in Sarcoplasmic Reticulum in Skeletal MusclesJournal of Molecular Biology, 2011
- Alteration of Sarcoplasmic ReticulumRelease in Skeletal Muscle from Calpain 3-Deficient MiceInternational Journal of Cell Biology, 2009
- Calpain 3, the “gatekeeper” of proper sarcomere assembly, turnover and maintenanceNeuromuscular Disorders, 2008
- Novel role of calpain-3 in the triad-associated protein complex regulating calcium release in skeletal muscleHuman Molecular Genetics, 2008
- Calpain 3 is a modulator of the dysferlin protein complex in skeletal muscleHuman Molecular Genetics, 2008
- Analysis of Relative Gene Expression Data Using Real-Time Quantitative PCR and the 2−ΔΔCT MethodMethods, 2001